March 5, 2012 - There are close to seven-thousand rare diseases, affecting about 25 million Americans and this week, families are coming together in Washington DC to raise awareness for rare diseases. Sanfilippo Syndrome is a metabolic disease that causes severe neurological damage that gets progressively worse. It causes the loss of ability to walk, talk and eat while the body shuts down. In the United States, they are 18 children with Sanfilippo subtype-c and nobody with it has lived past the age of 30. Sanfilippo Syndrome is inherited as an autosomal recessive trait. That means both your parents must pass you the defective gene in order for you to get the disease.
The FDA announced the entire class of statin drugs will get new labels that alert the public to safety concerns. Statins, used to lower high cholesterol, will now come with a warning that they can cause memory loss and confusion. The new labels will also warn doctors and patients that statins can cause an increase in blood sugar levels and increase the risk of Type 2 diabetes. Some of the products that will have these label changes include Lipitor, Crestor and Zocor. Nearly 32 million Americans are on statins.